Fragile X Clinical Trials

Jan 1 2013
Jan 1 2014
America/New York
Institute for Basic Research/ The Seaver Autism Center

New York Fragile X Clinical Trials Accepting Participants

(The following are four separate trials): 


Trials at IBR (Institute for Basic Research) on Staten Island

  • IBR on Staten Island is now screening adolescents as well as adults for a trial of AFQ056 from Novartis.  Males aged 12-45 who have Fragile X may be eligible.  This trial runs for 4 months and offers an extension phase in which participants can take the drug free of charge.
  • IBR is also running a trial of arbaclofen from Seaside Therapeutics for boys and girls ages 5-11 who have Fragile X; this trial includes an extension phase as well.  Seaside has completed enrollment for their trials of arbaclofen for ages 12-50.

Contact Information:

Principal Investigator Dr. Angelo Porto at IBR or 718-494-8028



Trials at the Seaver Autism Center at Mt. Sinai Medical Center

  • The Seaver Autism Center at Mt. Sinai Medical Center in Manhattan is offering the arbaclofen trial for ages 5-11 with the extension phase.
  • Mt. Sinai is recruiting men and women ages 16-50 with Fragile X for a large-scale trial Roche's experimental new drug code-named R04917523.  

Contact Information:

Clinical Research Coordinator Lauren Bush or 212-241-2826



For more information: